Cytokinetics Reports Third Quarter 2024 Financial Results
CYTK 11.06.2024

About Gravity Analytica
Rolling Submission of NDA for Aficamten Completed and Submitted to FDA in Q3
COMET-HF, Confirmatory Phase 3 Clinical Trial of Omecamtiv Mecarbil,and AMBER-HFpEF, Phase 2 Clinical Trial of CK-586, Expected to Begin in Q4
Plan to Advance CK-089, Fast Skeletal Muscle Troponin Activator,into First-In-Human Study in Q4 2024
“The progress we made in the third quarter reflects disciplined planning and prudent capital deployment throughout 2024 that has laid the foundation for our specialty cardiology business. The submission of the NDA foraficamtenis an important regulatory milestone that brings us one step closer to the potential approval and commercial launch ofaficamtenin
Q3 and Recent Highlights
Cardiac Muscle Programs
aficamten(cardiac myosin inhibitor)
- Completed the rolling submission of the New Drug Application (NDA) foraficamtenand submitted the NDA for the treatment of obstructive hypertrophic cardiomyopathy (HCM).
- Presented additional results from SEQUOIA-HCM (Safety,Efficacy, andQuantitativeUnderstanding ofObstructionImpact ofAficamteninHCM) at the
European Society of Cardiology 2024Congress ,Heart Failure Society of America (HFSA) Annual Scientific Meeting and Hypertrophic Cardiomyopathy Medical Society Scientific Sessions. Collectively, the data showed that treatment withaficamtenin SEQUOIA-HCM was associated with improvements in cardiac structure and function, heart failure symptoms, cardiac biomarkers, and multiple assessments of clinical significance to cardiologists. - Presented additional data related to the longer-term use ofaficamtenat the
European Society of Cardiology 2024Congress from an integrated safety analysis of three clinical studies ofaficamtenthat reinforced the robust safety profile ofaficamten. Additionally, an analysis from FOREST-HCM (Follow-up,Open-Label,ResearchEvaluation ofSustainedTreatment withAficamteninHCM,) the open label extension clinical study ofaficamtenin patients with HCM, demonstrated that patients who attempted withdrawal of standard of care medications did not experience negative impacts on the efficacy or safety ofaficamten. - Continued
U.S. commercial readiness activities foraficamtenincluding selecting third-party external partners for our bespoke patient support programs and distribution strategy, refining our sales force strategy, engaging with payers through pre-approval information exchange and developing ourU.S. value dossier. Launched “HCM Beyond the Heart,” an unbranded disease awareness campaign for healthcare professionals highlighting the holistic burden of HCM. - Continued preparing a Marketing Authorization Application (MAA) foraficamten, expected to be submitted to the
European Medicines Agency (EMA) and National Agencies in the EU in Q4 2024. - Continued European commercial readiness activities including designing the distribution model, refining regulatory and labeling strategies, establishing country launch sequencing, and engaging with European key opinion leaders. Established initial go-to-market plans for
Germany , the first potential European market launch.
- Corxel (formerly
Ji Xing Pharmaceuticals ) completed submission of the NDA foraficamtento treat obstructive HCM, which was accepted by theCenter for Drug Evaluation (CDE) of theNational Medical Products Administration (NMPA) inChina . - Completed enrollment in MAPLE-HCM (Metoprolol vsAficamteninPatients withLVOT Obstruction onExercise Capacity inHCM), the Phase 3 clinical trial comparingaficamtenas monotherapy tometoprololas monotherapy in patients with symptomatic obstructive HCM. We expect to report topline results from MAPLE-HCM in 1H 2025.
- Continued enrolling patients in ACACIA-HCM (AssessmentComparingAficamtento Placebo onCardiac EndpointsInAdults with Non-ObstructiveHCM), the pivotal Phase 3 clinical trial ofaficamtenin patients with non-obstructive HCM. We expect to complete enrollment in ACACIA-HCM in 2025.
- Continued patient enrollment in CEDAR-HCM (ClinicalEvaluation ofDosing withAficamtentoReduce Obstruction in a Pediatric Population inHCM), a clinical trial ofaficamtenin a pediatric population with symptomatic obstructive HCM. We expect to continue enrollment in CEDAR-HCM throughout 2024.
- Published the following manuscripts:
- “Dosing and Safety Profile ofAficamtenin Symptomatic Obstructive Hypertrophic Cardiomyopathy: Results From SEQUOIA-HCM” in the
Journal of the American Heart Association - “Effect ofAficamtenon Cardiac Structure and Function in Obstructive Hypertrophic Cardiomyopathy: SEQUOIA-HCM CMR Substudy” in the
Journal of the American College of Cardiology - “Impact ofAficamtenon Echocardiographic Cardiac Structure and Function in Symptomatic Obstructive Hypertrophic Cardiomyopathy” in the
Journal of the American College of Cardiology - “Effect ofAficamtenon Health Status Outcomes in Obstructive Hypertrophic Cardiomyopathy: Results from SEQUOIA-HCM” in the
Journal of the American College of Cardiology - “Cardiac Biomarkers and Effects ofAficamtenin Obstructive Hypertrophic Cardiomyopathy: the SEQUOIA-HCM Trial” in the
European Heart Journal - “Aficamtenand Cardiopulmonary Exercise Test Performance A Substudy of the SEQUOIA-HCM Randomized Clinical Trial” in the
Journal of the American Medical Association Cardiology - “Impact ofAficamtenon Disease and Symptom Burden in Obstructive Hypertrophic Cardiomyopathy: Results from SEQUOIA-HCM” in the
Journal of the American College of Cardiology - “Aficamten, a Novel and Selective Small-molecule Cardiac Myosin Inhibitor for the Treatment of Hypertrophic Cardiomyopathy” in
Nature Cardiovascular Research - “Pharmacokinetics, Excretion, and Metabolism of [14C]AficamtenFollowing Single Oral Dose Administration to Rats” inXenobiotica
- “In VitroandIn VivoPharmacokinetic Preclinical Characterization ofAficamten, a Small Molecule Cardiac Myosin Inhibitor” inXenobiotica
- “Pharmacokinetics, Disposition and Biotransformation of the Cardiac Myosin InhibitorAficamtenin Humans” in
Pharmacology Research and Perspectives - “Qualitative Interview Study of Patient-reported Symptoms, Impacts and Treatment Goals of Patients With Obstructive Hypertrophic Cardiomyopathy” in
British Medical Journal : Open Heart - “An Evidence Review and Gap Analysis for Obstructive Hypertrophic Cardiomyopathy” inBMC Cardiovascular Disorders
- “Differences in Healthcare Resource Use and Cost by Pharmacotherapy Among Patients with Symptomatic Obstructive Hypertrophic Cardiomyopathy: Real-World Analysis of Claims Data” in the
American Journal of Cardiovascular Drugs
- “Dosing and Safety Profile ofAficamtenin Symptomatic Obstructive Hypertrophic Cardiomyopathy: Results From SEQUOIA-HCM” in the
omecamtiv mecarbil(cardiac myosin activator)
- Conducted start-up activities for COMET-HF (Confirmation ofOmecamtivMecarbilEfficacyTrial inHeartFailure), a confirmatory Phase 3 multi-center, double-blind, randomized, placebo-controlled trial to assess the efficacy and safety ofomecamtiv mecarbilin patients with symptomatic heart failure with severely reduced ejection fraction, expected to start in Q4 2024.
CK-4021586(CK-586, cardiac myosin inhibitor)
- Presented data from the Phase 1 study of CK-586 at the
American College of Clinical Pharmacology (ACCP) Annual Meeting. The study met its primary and secondary objectives to assess the safety, tolerability and pharmacokinetics of single and multiple oral doses of CK-586. - Conducted start-up activities for AMBER-HFpEF (Assessment of CK-586 in aMulti-Center,BlindedEvaluation of Safety and TolerabilityResults inHFpEF), a Phase 2 randomized, placebo-controlled, double-blind, multi-center, dose-finding clinical trial in patients with symptomatic heart failure with preserved ejection fraction (HFpEF) with left ventricular ejection fraction (LVEF) ≥ 60%, expected to start in Q4 2024.
- Expect to advance CK-4015089 (CK-089), a fast skeletal muscle troponin activator (FSTA) with potential therapeutic application to a specific type of muscular dystrophy, into a first-in-human Phase 1 study in Q4 2024.
- Continued pre-clinical development and research activities directed to additional muscle biology focused programs.
Corporate
- Announced a call for proposals for the Cytokinetics Corporate Giving Program. The program provides charitable donations to eligible non-profit organizations in
the United States to support diversity in science education, equitable healthcare initiatives for cardiovascular disease and certain essential services for local and at-risk communities. - Announced a call for proposals for the seventh annual Cytokinetics Communications Grant Program. The program awards five grants to patient advocacy organizations serving the HCM or heart failure communities and is intended to support increased capacity in communications and outreach.
Third Quarter 2024 Financial Results
Cash, Cash Equivalents and Investments
- As of
September 30, 2024 , the company had approximately$1.3 billion in cash, cash equivalents and investments compared to$1.4 billion atJune 30, 2024 . Cash, cash equivalents and investments declined by approximately$81 million during the third quarter of 2024.
Revenues
- Total revenues for the third quarter of 2024 were
$0.5 million compared to$0.4 million for the same period in 2023.
Research and Development (R&D) Expenses
- R&D expenses for the third quarter of 2024 were
$84.6 million which included$11.4 million of non-cash stock-based compensation expense, compared to$82.5 million for the same period in 2023 which included$8.2 million of non-cash stock-based compensation expense. The increase was primarily driven by higher personnel related expenses to progress our pipeline partially offset by the completion of clinical trials.
General and Administrative (G&A) Expenses
- G&A expenses for the third quarter of 2024 were
$56.7 million which included$13.9 million of non-cash stock-based compensation expense, compared to$40.1 million for the same period in 2023 which included$10.5 million in non-cash stock-based compensation expense. The increase was primarily driven by investments toward commercial readiness and personnel related expenses.
Net Income (Loss)
- Net loss for the third quarter of 2024 was
$160.5 million , or$(1.36) per share, basic and diluted, compared to a net loss of$129.4 million , or$(1.35) per share, basic and diluted, for the same period in 2023.
2024 Financial Guidance
The company is reiterating its full year 2024 financial guidance:
2024 Guidance | |
GAAP Operating Expense[1] | |
Non-cash Expense[2]Included in GAAP Operating Expense | |
Non-GAAP Operating Expense[3] | |
Net Cash Utilization[4] |
The financial guidance does not include the effect of GAAP adjustments as may be caused by events that occur subsequent to publication of this guidance including but not limited to Business Development activities.
[1]GAAP operating expense comprised of R&D and G&A expenses.[2]Non-cash operating expense comprised of stock-based compensation and depreciation.[3]Non-GAAP operating expense comprised of R&D and G&A expenses but excludes non-cash operating expense.[4]Net cash utilization is a non-GAAP financial measure that we define as our ending 2023 cash, cash equivalents, and investments balance of
Conference Call and Webcast Information
Members of Cytokinetics’ senior management team will review the company’s third quarter 2024 results on a conference call today at
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Forward-Looking Statements
This press release contains forward-looking statements for purposes of the Private Securities Litigation Reform Act of 1995 (the “Act”).
CYTOKINETICS® and the
Contact:
Condensed Consolidated Balance Sheets | |||||||
(in thousands) | |||||||
(unaudited) | |||||||
ASSETS | |||||||
Current assets: | |||||||
Cash and short term investments | $ | 1,011,692 | $ | 614,824 | |||
Other current assets | 6,909 | 13,227 | |||||
Total current assets | 1,018,601 | 628,051 | |||||
Long-term investments | 269,168 | 40,534 | |||||
Property and equipment, net | 64,222 | 68,748 | |||||
Operating lease right-of-use assets | 76,344 | 78,987 | |||||
Other assets | 7,725 | 7,996 | |||||
Total assets | $ | 1,436,060 | $ | 824,316 | |||
LIABILITIES AND STOCKHOLDERS’ DEFICIT | |||||||
Current liabilities: | |||||||
Accounts payable and accrued liabilities | $ | 61,407 | $ | 64,148 | |||
Short-term operating lease liabilities | 18,856 | 17,891 | |||||
Current portion of long-term debt | 11,520 | 10,080 | |||||
Derivative liabilities measured at fair value | 12,500 | — | |||||
Other current liabilities | 5,529 | 10,559 | |||||
Total current liabilities | 109,812 | 102,678 | |||||
Term loan, net | 93,017 | 58,384 | |||||
Convertible notes, net | 551,481 | 548,989 | |||||
Liabilities related to revenue participation right purchase agreements, net | 448,509 | 379,975 | |||||
Long-term operating lease liabilities | 114,752 | 120,427 | |||||
Liabilities related to RPI Transactions measured at fair value | 132,400 | — | |||||
Other non-current liabilities | — | 186 | |||||
Total liabilities | 1,449,971 | 1,210,639 | |||||
Commitments and contingencies | |||||||
Stockholders' deficit | |||||||
Common stock | 118 | 102 | |||||
Additional paid-in capital | 2,532,328 | 1,725,823 | |||||
Accumulated other comprehensive income (loss) | 5,387 | (10 | ) | ||||
Accumulated deficit | (2,551,744 | ) | (2,112,238 | ) | |||
Total stockholders' deficit | (13,911 | ) | (386,323 | ) | |||
Total liabilities and stockholders' deficit | $ | 1,436,060 | $ | 824,316 | |||
Condensed Consolidated Statements of Operations | |||||||||||||||
(in thousands except per share data) | |||||||||||||||
(unaudited) | |||||||||||||||
Three Months Ended | Nine Months Ended | ||||||||||||||
Revenues: | |||||||||||||||
Research and development revenues | $ | 463 | $ | 378 | $ | 1,547 | $ | 3,358 | |||||||
Milestone revenues | — | — | — | 2,500 | |||||||||||
Total revenues | 463 | 378 | 1,547 | 5,858 | |||||||||||
Operating expenses: | |||||||||||||||
Research and development | 84,612 | 82,532 | 245,779 | 245,147 | |||||||||||
General and administrative | 56,652 | 40,111 | 152,976 | 129,498 | |||||||||||
Total operating expenses | 141,264 | 122,643 | 398,755 | 374,645 | |||||||||||
Operating loss | (140,801 | ) | (122,265 | ) | (397,208 | ) | (368,787 | ) | |||||||
Interest expense | (8,928 | ) | (7,136 | ) | (28,763 | ) | (21,142 | ) | |||||||
Non-cash interest expense on liabilities related to revenue participation right purchase agreements | (13,370 | ) | (6,860 | ) | (35,155 | ) | (19,462 | ) | |||||||
Interest and other income, net | 17,054 | 6,839 | 36,520 | 20,043 | |||||||||||
Change in fair value of derivative liabilities | 700 | — | 100 | — | |||||||||||
Change in fair value of liabilities related to RPI Transactions | (15,200 | ) | — | (15,000 | ) | — | |||||||||
Net loss | $ | (160,545 | ) | $ | (129,422 | ) | $ | (439,506 | ) | $ | (389,348 | ) | |||
Net loss per share — basic and diluted | $ | (1.36 | ) | $ | (1.35 | ) | $ | (4.00 | ) | $ | (4.07 | ) | |||
Weighted-average number of shares used in computing net loss per share — basic and diluted | 117,685 | 96,071 | 109,932 | 95,666 | |||||||||||

Source: Cytokinetics, Incorporated